Disease

Familial thrombotic thrombocytopenic purpura1, 2

Gene

ADAMTS13

Inheritance AR
Current Treatments Plasma infusion or exchange. Adzynma (recombinant ADAMTS13)
Evidence for Treatment guideline3
Non-Molecular Testing Availability yes
Non-Molecular Test ADAMTS13 activity4
Experimental / Investigational Therapies https://clinicaltrials.gov/ct2/results?cond=ADAMTS13&term=&cntry=&state=&city=&dist=
Last Updated: March 5, 2026
RX Genes
Privacy Overview

This website uses cookies so that we can provide you with the best user experience possible. Cookie information is stored in your browser and performs functions such as recognising you when you return to our website and helping our team to understand which sections of the website you find most interesting and useful.